Tag: Rare Diseases

Market News

UniQure Seeks FDA Approval for Huntington’s Gene Therapy

After months of public tension with regulators, UniQure is moving forward with its Huntington's gene therapy application. The stunning turnaround...

17/06/2026

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Market News

Rare Disease Families Find New Hope Through Drug Development Bootcamps

When parents hear their child has a rare disease with no treatment, most feel powerless. But a growing number are...

11/05/2026

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Market News

Revolutionizing Rare Disease Care With Drug Repurposing

Imagine finding effective treatments for rare diseases not by creating expensive new drugs, but by rediscovering what's already on pharmacy...

28/03/2026

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Market News

How CNBC Cures Elevates Rare Disease Awareness

Behind the camera, a well-known journalist shares her daughter's battle with a rare genetic condition. What started as personal pain...

21/03/2026

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Market News

FDA Reversals Raise Biotech Investor Concerns

The FDA's sudden shifts on drug approvals have biotech investors rattled. After pledging more flexibility for rare diseases, recent denials...

06/03/2026

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Market News

FDA Chaos: Staff Losses Threaten Rare Disease Drugs

The FDA is hemorrhaging experienced staff and facing accusations of chaos, leading to stalled approvals for desperately needed rare disease...

04/03/2026

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Market News

Rare Disease Stories: Families Fighting for Hope

When a child's rare disease turns life upside down, families refuse to give up. From launching foundations to chasing experimental...

11/02/2026

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Global Markets

US Biotech Leadership Vital for Rare Disease Breakthroughs

As China surges in biotechnology, rare disease patients face an uncertain future. Will the US maintain its edge in life-saving...

16/01/2026

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Market News

CNBC Cures Launches to Support Rare Disease Community

When a journalist shared her daughter's rare disease battle, the response was overwhelming. Thousands signed up, stories poured in. But...

12/01/2026

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Market News

CNBC Launches Initiative for Rare Diseases

Thirty million Americans live with rare diseases, often facing years of uncertainty before a diagnosis. Now, a major network is...

08/01/2026

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